Duchenne muscular dystrophy: advances in therapeutics

 Content: 1. Clinical overview of Duchenne muscular dystrophy / Richard T. Moxley III --
 2. functional biology of dystrophin: structural components and the pathogenesis of Duchenne muscular dystrophy / Eijiro Ozawa --
 3. functional biology of dystrophin: associated signaling pathways and potential targets for therapeutic intervention / Gayle Smythe, Steven J. Winder and Thomas A. Rando --
 4. Duchenne muscular dystrophy and Becker muscular dystrophy: diagnostic principles / H. B. Ginjaar, J. T. den Dunnen, E. Bakker and G. J. B. van Ommen --
 5. Mutation detection / Thomas W. Prior --
 6. Protein studies in Duchenne muscular dystrophy / Kathryn North and Sandra Cooper --
 7. Medical management of Duchenne muscular dystrophy / Roula Al-Dahhak and John T. Kissel --
 8. Rehabilitation management of Duchenne muscular dystrophy / Craig M. McDonald, Gregory T. Carter, Jay J. Han and Joshua O. Benditt --
 9. Orthopedic interventions in the management of Duchenne muscular dystrophy: a review of current practice and clinical outcomes / Irwin M. Siegel and John D. Hsu --
 10. Therapeutic principles and challenges in Duchenne muscular dystrophy / Dominic J. Wells --
 11. Experimental pharmacologic therapies in Duchenne dystrophy: current clinical trials / Shannon L. Venance and Robert C. Griggs --
 12. Utrophin: the intersection between pharmacological and genetic therapy / Kelly J. Perkins and Kay E. Davies --
 13. Regenerative therapy / J. E. Morgan, Karima Brimah, C. A. Collins and T. A. Partridge --
 14. Cellular mediated delivery: the intersection between regenerative medicine and genetic therapy / K. Liadaki, F. Montanaro and L. M. Kunkel --
 15. Oligonucleotide-mediated exon skipping and gene editing for Duchenne muscular dystrophy / Carmen Bertoni and Thomas A. Rando --
 16. intravascular delivery of naked DNA for treating Duchenne muscular dystrophy / Jon A. Wolff and Hans Herweijer --
 17. Adenoviral-mediated gene therapy / Laura Goldberg and Paula R. Clemens --
 18. Retroviridae-based gene transfer vectors in Duchenne muscular dystrophy therapy / Michael L. Roberts, George Dickson and Michael Themis --
 19. Gene therapy of muscular dystrophy using adeno-associated viral vectors: promises and limitations / Michael J. Blankinship, Paul Gregorevic and Jeffrey S. Chamberlain --
 20. Regional and systemic gene delivery using viral vectors / Leonard T. Su and Hansell H. Stedman.